PipelineHuidaGene has multiple R&D pipelines for ophthalmology and neurology.
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01Neurology Diseases
MECP2 Duplication Syndrome (MDS)
Huntington's Disease (HD)
Amyotrophic Lateral Sclerosis (ALS)
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02Ophthalmology Diseases
RPE65 Mutation-Associated Inherited Retinal Dystrophies (RPE65-IRD)
Neovascular Age-related Macular Degeneration (nAMD)
RHO-Associated Retinitis Pigmentosa (RHO-adRP)
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03Neuromuscular Diseases
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FDA Awards Orphan Drug and Rare Pediatric Disease Designations to the World’s First Cas13X RNA Base-editing Therapy for the Treatment of Congenital Hearing LossApr 15,2024
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HuidaGene Therapeutics to Open Up the First CRISPR MEDiCiNE European ConferenceApr 15,2024
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HuidaGene's Sixteen Abstracts Highlight the Strength of the Pipeline and Platform to Advance Genetic Medicines at the 2024 ASGCT Annual MeetingApr 08,2024
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